Infantile-onset multisystem autoimmune disease (ADMIO) is typified by hypogammaglobulinemia and onset of autoimmune phenomena during early childhood that include diabetes and autoimmune enteritis.
Category
Immune system disease
Brite
Human diseases [BR:br08402]
Immune system diseases
Allergies and autoimmune diseases
H02540 Infantile-onset multisystem autoimmune disease
Human diseases in ICD-11 classification [BR:br08403]
04 Diseases of the immune system
Nonorgan specific systemic autoimmune disorders
4A43 Overlap or undifferentiated nonorgan specific systemic autoimmune disease
H02540 Infantile-onset multisystem autoimmune disease
Flanagan SE, Haapaniemi E, Russell MA, Caswell R, Allen HL, De Franco E, McDonald TJ, Rajala H, Ramelius A, Barton J, Heiskanen K, Heiskanen-Kosma T, Kajosaari M, Murphy NP, Milenkovic T, Seppanen M, Lernmark A, Mustjoki S, Otonkoski T, Kere J, Morgan NG, Ellard S, Hattersley AT
Title
Activating germline mutations in STAT3 cause early-onset multi-organ autoimmune disease.
Journal
Nat Genet 46:812-814 (2014) DOI:10.1038/ng.3040
Reference
PMID:26783323
Authors
Chan AY, Punwani D, Kadlecek TA, Cowan MJ, Olson JL, Mathes EF, Sunderam U, Fu SM, Srinivasan R, Kuriyan J, Brenner SE, Weiss A, Puck JM
Title
A novel human autoimmune syndrome caused by combined hypomorphic and activating mutations in ZAP-70.
Journal
J Exp Med 213:155-65 (2016) DOI:10.1084/jem.20150888
Reference
PMID:31771449
Authors
Terry J, Langlois S, Rupps R, Gill H
Title
Prenatal Autoimmune Disease, Multisystem, Infantile Onset-like Phenotype and Proximal Renal Tubular Dysplasia Associated With STAT3 Mutation.
Journal
Pediatr Dev Pathol 23:306-311 (2020) DOI:10.1177/1093526619890734