DISEASE: Autoinflammation, immune dysregulation, and eosinophilia
Entry
H02537 Disease
Name
Autoinflammation, immune dysregulation, and eosinophilia
Description
Autoinflammation, immune dysregulation, and eosinophilia (AIIDE) is an autosomal dominant systemic immune dysregulatory syndrome caused by gain-of-function mutations in JAK1. JAK-STAT signaling pathway plays an integral role in extracellular cytokine and growth factor signaling, as well as in controlling hematopoiesis and immune function. It has been reported that AIIDE is rescued by JAK inhibitor therapy.
Category
Immune system disease
Brite
Human diseases [BR:br08402]
Immune system diseases
Allergies and autoimmune diseases
H02537 Autoinflammation, immune dysregulation, and eosinophilia
Human diseases in ICD-11 classification [BR:br08403]
04 Diseases of the immune system
Nonorgan specific systemic autoimmune disorders
4A4Y Other specified nonorgan specific systemic autoimmune disorders
H02537 Autoinflammation, immune dysregulation, and eosinophilia
Related pathway
hsa04630
JAK-STAT signaling pathway
hsa04658
Th1 and Th2 cell differentiation
hsa04659
Th17 cell differentiation
Gene
JAK1 [HSA:3716] [KO:K11217]
Other DBs
ICD-11:
4A4Y
MeSH:
D056660
OMIM:
618999
Reference
PMID:28111307
Authors
Del Bel KL, Ragotte RJ, Saferali A, Lee S, Vercauteren SM, Mostafavi SA, Schreiber RA, Prendiville JS, Phang MS, Halparin J, Au N, Dean JM, Priatel JJ, Jewels E, Junker AK, Rogers PC, Seear M, McKinnon ML, Turvey SE
Title
JAK1 gain-of-function causes an autosomal dominant immune dysregulatory and hypereosinophilic syndrome.