Sulfonic acid analog of γ-aminobutyric acid (GABA), q.v. Binds to soluble amyloid β peptide (Aβ), q.v., and inhibits fibrillization and plaque formation. Prepn: S. Gabriel, W. E. Lauer, Ber. 23, 87 (1890); P. Rumpf, Compt. Rend. 204, 592 (1937). Large scale synthesis from 1,3-propane sultone: X. Kong et al., WO 04113391; eidem, US 050143462 (2004, 2005 both to Neurochem). Crystal structure: K. Tomita, Tetrahedron Lett. 12, 2587 (1971) DOI. GABA mimetic activity: R. G. Fariello, G. T. Golden, Brain Res. Bull. 5, Suppl. 2, 691 (1980) DOI. Pharmacology and binding to Aβ: F. Gervais et al., Neurobiol. Aging 28, 537 (2007) DOI PubMed. Pharmacokinetics in patients with cerebral amyloid angiopathy: S. M. Greenberg et al., Alzheimer Dis. Assoc. Disord. 20, 269 (2006) DOI PubMed. Clinical effect on Aβ42 levels in CSF of Alzheimer's patients: P. S. Aisen et al., Neurology 67, 1757 (2006) DOI PubMed.
Antiamyloidogenic agent; in treatment of Alzheimer's disease.
Antiamyloidogenic