DNA alkylating and crosslinking agent. Bifunctional sulfonylhydrazine prodrug that generates a chloroethylating species, VPN-4090CE, and methyl isocyanate, q.v., a carbamoylating agent. Prepn: A. Sartorelli et al., WO 9702029; eidem, US 5637619 (both 1997 to Yale); K. Shyam et al., J. Med. Chem. 39, 796 (1996) DOI PubMed. Analytical methods and formulation: G. Krishna et al., AAPS PharmSciTech 2 (3), 39-47 (2001) DOI. LC-ESI-MS/MS determn in plasma: F. Bai et al., J. Chromatogr. B 853, 97 (2007) DOI. Mechanism of action: K. Ishiguro et al., Mol. Cancer Ther. 5, 969 (2006) DOI PubMed; P. G. Penketh et al., Leuk. Res. 32, 1546 (2008) DOI PubMed. Clinical evaluation in recurrent glioblastoma multiforme: M. A. Badruddoja et al., Neuro Oncol. 9, 70 (2007) DOI PubMed; in acute myeloid leukemia: F. Giles et al., J. Clin. Oncol. 25, 25 (2007) DOI PubMed.
Prepn: K. Shyam et al., J. Med. Chem. 33, 2259 (1990).
Antineoplastic.
Antineoplastic; Alkylating Agents